嘉宾名单(按字母顺序排列)
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Brian K KASPAR, Ph. D, Chief Scientific Officer, AVEXIS Inc., USA Brian K KASPAR, 博士,教授,基因治疗中心及神经生物学系,美国全国儿童医院及研究中心
KASPAR的实验室研究方向是肌萎缩性脊髓侧索硬化症(ALS)及脊髓性肌萎缩症(SMA)的神经退行性病变机制。同时,该实验室针对肌肉系统的研究推动了骨骼肌系统疾病治疗的发展。基于该实验室腺病毒研究的贝克肌营养不良(Becker Muscular Dystrophy)及包涵体肌炎(Inclusion Body Myositis)一期、二期临床试验正在进行中。此外,该实验室在SMA基因治疗的临床试验方面取得了较大进展。
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Brian R. ROBINSON, MD, Vice President, Medical Affairs, Bluebirdbio, USA
Brian Robinson, 医学博士,美国Bluebird bio副总裁、医学事务总监 |
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Chen LI, MD, Peking Union Medical College
李忱,医学博士,主治医师,北京协和医院 |
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Cheng-hua LEE, Ph.D., Deputy Director General, National HealthInsurance Administration Ministry of Health and Welfare, Taiwan, China
李丞华,博士,台湾卫生福利部中央健康保险署副署长,台湾阳明大学医务管理研究所兼任教授 |
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Christina WATERS, Ph. D, MBA, President/CEO/Founder, RARE Science Inc., USA
Christina Waters, 博士,工商管理硕士,RARE Science 首席执行官 |
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Francis X. McCormack, MD, Professor, Department of Internal Medicine, University of Cincinnati School of Medicine, USA
Francis McCormack,医学博士,美国辛辛那提大学内科学教授,肺,重症监护与睡眠医学科室主任
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Guangping GAO, Ph.D, Professor, Microbiology & Physiological Systems, Penelope Booth Rockwell Professor in Biomedical Research, Director, Horae GeneTherapy Center and Vector Core, University of Massachusetts Medical School, USA
Guangping Gao,博士,微生物及生理学系教授,红瑞(Horae)基因治疗中心主任,美国麻省州立大学医学院 Gao 博士共计发表期刊文章212篇,编辑出版专著5本,拥有121项专利,部分授权给十余家药厂投产,此外,还有215项专利在申请中。Gao 博士是Human Gene Therapy主编,Gene and Cell Therapy系列丛书高级编辑,Signal Transduction and Targeted Therapy副主编,Advances in Experimental Medicine and Biology顾问,美国基因及细胞治疗学会(American Society of Gene and Cell Therapy)理事会成员及学会副主席,Gene Therapy、Molecular and Cellular Therapy、 Journal of Neurological Disorders、Current Opinion in Virology等学术期刊的编委会成员,美国国立卫生研究院(NIH)及其他美国、国际研究机构的常委会成员。Gao 博士是生物制药企业Voyager Therapeutics(位于坎布里奇,美国马塞诸萨州)的创始人之一,致力于研发针对中枢神经系统疾病的rAAV基因治疗方案。 |
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Harvey F. LODISH, Ph. D, Professor of Biology and Professor of Bioengineering, Massachusetts Institute of Technology, USA
Harvey Lodish,博士,Whitehead 生物医学研究所创始人之一,美国麻省理工学院生物学教授,生物工程学教授 |
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Kevin Rufang HUANG, President of Chinese Organization for Rare Disorders, China
黄如方,罕见病发展中心创始人/主任 |
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Manuel POSADA, Director, Institute of Rare Diseases Research, ISCIII & President of ICORD, Spain |
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Mark J. PYKETT, VMD, MD, Presidet/CEO, Agilis Biotherapeutics,USA
Mark Pykett,兽医博士,博士,工商管理硕士,美国Agilis生物制药公司总裁兼首席执行官 |
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Meryem NIMOUR, MD, Vice President, Medical Affairs for Rare Disease in Emerging Markets, Pfizer, USA
Meryem Nimour,医学博士,美国辉瑞公司新兴市场罕见病医疗部副总裁 |
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Mengchun GONG, MD, Executive Director, National Rare Disease Registry System, China
弓孟春,医学博士,中国医学科学院罕见病研究中心项目办公室主任及国家罕见病注册研究体系执行总监 |
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Raman RAJAKANTH, Executive Director, Rainbow Across Border, Singapore
Raman RAJAKANTH, 新加坡罕见病组织“跨越国界的彩虹”执行董事 |
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Renchi YANG, MD, Director, Institute of Hematology, Chinese Academy of Medical Sciences, China
杨仁池,医学博士,中国医学科学院血液病医院血栓止血诊疗中心主任 |
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Shuyang ZHANG, Vice President, Peking Union Medical College Hospital, China
张抒扬,主任医师,教授,北京协和医院副院长兼中国医学科院北京协和医学院副院校长,北京协和医院药理研究中心主任,转化医学研究中心副主任 |
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Terence R.FLOTTE, MD, Provost, Dean and Professor, Horae Gene Therapy Center, University of Massachusetts Medical School, USA
Terence R. Flotte,博士,美国马萨诸塞大学医学院院长,教务长,Horae基因治疗中心教授 |
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Wendy CHUNG, MD, PhD, Kennedy Family Professor of Pediatrics and Medicine, Columbia University, USA
Wendy Chung, 医学博士,博士,美国哥伦比亚大学医学中心儿科学与内科学肯尼迪家族教授 |
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Xiaochun LIANG, Professor, Director of Chinese Traditional Medicine, Peking Union Medical College Hospital, China
梁晓春,北京协和医院中医科主任、教授、博士生导师 |
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Xuefan GU, MD, Ph.D,Vice President, Director, Xin Hua Hospital Affiliated to Shanghai Jiaotong University, China
顾学范,主任医师、教授、研究员、博士生导师,上海市儿科医学研究所副所长 |
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Yaping YANG, Ph. D, FACMG, Baylor Genetics, Baylor College of Medicine, USA
杨亚平,博士,贝勒遗传学实验室下一代测序(NGS)部门主任;美国贝勒医学院副教授 |
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Wei ZHANG, Ph.D, Director of AmCare Genomics Laboratory, China
张巍,博士,广州嘉检医学医学主任 现任美国贝勒医学院客座副教授,南方医科大学客座教授,复旦大学儿科医院客座教授,广州嘉检医学医学主任,全国卫生产业企业管理协会实验医学专家委员。曾任美国贝勒医学院医学遗 传学实验室副主任、贝勒医学院助理教授。 |
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Zhenhua DONG, Professor, Chinese Traditional Medicine, Peking Union Medical College Hospital, China
董振华,教授,北京协和医院中医科 |
Ana RATH, Ph. D, Director, Orphanet, France (法国)
Durhane WANG-RIEGER, President, Canadian Organization for Rare Disorders, Canada(加拿大)
Hugh DAWKINS, Director of the Office of Population Health Genomics (OPHG), Public Health Division, Australia(澳大利亚)
Jianmin LIU 刘建民, Professor, Director of Endocrinology Department, RuiJin Hospital Shanghai Jiao Tong University of Medicine, China
Jim Green, President, International Niemann-Pick Disease Alliance, UK(英国)
Junshuai LIU 刘军帅, Labor and Social Security Office of Qingdao, China
Kaixian CHEN陈凯先,Academician of Chinese Academy of Science,professor of medicine,China
Ming QI 祁鸣, Professor of foundation medicine, Zhe Jiang University School of Medicine, China
Peter BAUER, Professor, Institute of Medical Genetics and applied Genomics, University Hospital Tübingen, Tübingen, Germany(德国)
Xiarong LI 李夏戎, Ph.D, CEO/founder, Genedock, China
Stephen C.GROFT, Pharm.D, Senior Advisor to the Director, National Center for Advancing Translational Sciences, NIH, USA(美国)
Tao DUAN 段涛, Professor, Chief Physician, Obstetrical Department, Shanghai First Maternity and Infant Hospital, China
Wenhao ZHOU 周文浩, Professor, Vice-President of Fudan University Pediatric Hospital, China
Weihong GU 顾卫红, Ph.D, China-Japan Friendship Hospital, China
Xue ZHANG 张学, professor,vice president, Graduate School of Peking Union Medical College Hospital, China
Yicheng ZHU 朱以诚, Professor, Vice Director of Neurology, Peking Union Medical College Hospital, China
Zhicheng JING 荆志成, Professor, Chief of Scientific Research Department, Fuwai Hospital, China