Confirmed Speakers:

Professor Marc Patterson, M.D., Chair,Division of Child and Adolescent Neurology, Mayo Clinic Children's Center, USA
Dr Teresa Wu,Principal Clinical Scientist, Manchester University Hospital Trust, Deputy Director at Willlink Biomedical Genetics, UK Professor Huiwen Zhang, M.D., Deputy Chief Physician, Department of Endocrine andGenetic Metablic Disease, Shanghai Xinhua Hospital, Shanghai Institute for Pediatric Research, China
Professor Melissa Wasserstein, M.D., (By video) Chief, Division of Pediatric Genetic Medicine, Department of Pediatrics , Associate Professor, Department of Pediatrics (Pediatric Genetic Medicine), Associate Professor, Department of Genetics,  The Children’s Hospital at Montefiore, New York, USA 
Dr. Xiangfeng Tang, M.D., Deputy Chief Physician, Pediatric Department, General Navy Hospital, Beijing, China

Target Attendees:

Treating Physicians for Niemann-Pick Disease, and/or Hereditary Metabolic Rare Disorders
Policy makers, patient organizations, industry representatives  

Meeting Registration:
    
Registered participants of ICORD 2017 meeting can attend the meeting for free
To register for the symposium alone, please register at ICORD 2017 meeting website. http://icord2017.medmeeting.org/Content/63573

AGENDA
Thursday, 7th September 2017

1.00 pm – 2.00  –    Meeting Registration
Meeting facilitator:  Ning Lü, Development Officer INPDA
2:00 pm – 2.15 pm –        Introductory Session  Chair:
Jim Green President INPDA    
Welcome on behalf of INPDA
Meeting – Structure and Objectives
2:15 pm – 2.25 pm –        Introductory Session  
Overview of Niemann Pick Disease Patients in China – Mrs. Zhang, Aijun, President CNPDA
2.25 pm – 3.45 pm     Session
1: Niemann Pick Diagnosis  
Current practice: NPD diagnosis in China (25 min) –
Professor Zhang, Huiwen   
Current practice: NPD diagnosis in the US/Europe (25 min) – Dr Teresa Wu
Current practice: NPD ASMD diagnosis in the US/Europe
Questions and panel discussions (30 min)
3.45 pm – 4.15 pm     Coffee and Refreshments
4.15 pm – 5:50 pm         Session 2: Clinical Management  
Clinical management of ASMD (25 min) –
Professor Melissa Wasserstein (Video Presentation) 
Clinical management of NPC (25 min) –Professor Marc Patterson
Questions and discussions (45min)  
Casestudy: Allogeneic hematopoietic stem cell transplantation for treating NPD patients – Dr. Xiangfeng Tang
Discussions of other ASMD and NPC clinical management practices
5.50 pm – 6:00 pm     Conclusions and closing remarks   - Professor Marc Patterson & Jim Green